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Introduction Hereditary transthyretin amyloidosis (hATTR) is a rare, multisystem genetic disorder resulting from the deposition of misfolded mutant transthyretin (TTR) protein in various organs (1). While patients often present with neurological and/or cardiac manifestations, nonspecific gastrointestinal symptoms related to autonomic dysfunction, a

Patisiran Treatment in Hereditary Transthyretin Amyloidosis Case
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